A phase 1 dose-escalation study: Safety, tolerability, and pharmacokinetics of FBS0701, a novel oral iron chelator for the treatment of transfusional iron overload

by Hugh Young Rienhoff, Vip Viprakasit, Lay Tay, Paul Harmatz, Elliott Vichinsky, Deborah Chirnomas, Janet L. Kwiatkowski, Amy Tapper, William Kramer, John B. Porter, Ellis J. Neufeld
Published 2018

Consensus statement for the perinatal management of patients with a thalassemia major

by Tippi C. MacKenzie, Ali Amid, Michael Angastiniotis, Craig Butler, Sandra Gilbert, Juan Gonzalez, Roberta L. Keller, Sandhya Kharbanda, Melanie Kirby-Allen, Barbara A. Koenig, Wade Kyono, Ashutosh Lal, Billie R. Lianoglou, Mary E. Norton, Keith K. Ogasawara, Tachjaree Panchalee, Mara Rosner, Marisa Schwab, Alexis Thompson, John S. Waye, Elliott Vichinsky
Published 2022