Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA

by Hansen, Bettina E., Vandriel, Shannon M., Vig, Pamela, Garner, Will, Mogul, Douglas B., Loomes, Kathleen M., Piccoli, David A., Rand, Elizabeth B., Jankowska, Irena, Czubkowski, Piotr, Gliwicz-Miedzinska, Dorota, Gonzales, Emmanuel M., Jacquemin, Emmanuel, Bouligand, Jerome, D'Antiga, Lorenzo, Nicastro, Emanuele, Arnell, Henrik, Fischler, Bjorn, Sokal, Etienne, Demaret, Tanguy, Siew, Susan, Stormon, Michael, Karpen, Saul J., Romero, Rene, Ebel, Noelle H., Feinstein, Jeffrey A., Roberts, Amin J., Evans, Helen M., Sundaram, Shikha S., Chaidez, Alexander, Hardikar, Winita, Shankar, Sahana, Fischer, Ryan T., Lacaille, Florence, Debray, Dominique, Lin, Henry C., Jensen, M. Kyle, Jaramillo, Catalina, Karthikeyan, Palaniswamy, Indolfi, Giuseppe, Verkade, Henkjan J., Larson-Nath, Catherine, Quiros-Tejeira, Ruben E., Valentino, Pamela L., Rogalidou, Maria, Dezsofi, Antal, Squires, James E., Schwarz, Kathleen, Calvo, Pier Luigi, Bernabeu, Jesus Quintero, Zizzo, Andreanne N., Nebbia, Gabriella, Bulut, Pinar, Santos-Silva, Ermelinda, Fawaz, Rima, Nastasio, Silvia, Karnsakul, Wikrom, Tamara, Maria Legarda, Busoms, Cristina Molera, Kelly, Deirdre A., Sandahl, Thomas Damgaard, Jimenez-Rivera, Carolina, Banales, Jesus M., Mujawar, Quais, Li, Li-Ting, She, Huiyu, Wang, Jian-She, Kim, Kyung Mo, Oh, Seak Hee, Sanchez, Maria Camila, Cavalieri, Maria Lorena, Lee, Way Seah, Hajinicolaou, Christina, Lertudomphonwanit, Chatmanee, Waisbourd-Zinman, Orith, Arikan, Cigdem, Alam, Seema, Carvalho, Elisa, Melere, Melina, Eshun, John, Onal, Zerrin, Desai, Dev M., Wiecek, Sabina, Pinto, Raquel Borges, Wolters, Victorien M., Garcia, Jennifer, Beretta, Marisa, Kerkar, Nanda, Brecelj, Jernej, Rock, Nathalie, Lurz, Eberhard, Blondet, Niviann, Shah, Uzma, Thompson, Richard J., Kamath, Binita M., GALA, Global Alagille Alliance
Published 2024