A randomized phase I/II trial of HQK-1001, an oral fetal globin gene inducer, in β-thalassaemia intermedia and HbE/β-thalassaemia

by Suthat Fucharoen, Adlette Inati, Noppadol Siritanaratku, Swee L. Thein, William C. Wargin, Suzanne Koussa, Ali Taher, Nattawara Chaneim, Michael Boosalis, Ronald Berenson, Susan P. Perrine
Published 2018