Non-ambulatory Duchenne muscular dystrophy: observations, interventions, and outcomes of a single case

Duchenne muscular dystrophy (DMD) is an X-linked recessive gene defect manifesting as a fatal, progressive neuromuscular disease. Treatment goals aim to inhibit disease progression, increase patients’ quality of life, and lengthen life expectancy. We report here a single case of non-ambulatory DMD....

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Bibliographic Details
Main Authors: Noer, Sevria Yetty Anggraina, Sunartini, Sunartini, Suryantoro, Purnomo
Format: Article PeerReviewed
Language:English
Published: Indonesian Pediatric Society Publishing House 2022
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Online Access:https://repository.ugm.ac.id/283792/1/2447-Article%20Text-11291-2-10-20220712%281%29.pdf
https://repository.ugm.ac.id/283792/
https://www.scopus.com/
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Institution: Universitas Gadjah Mada
Language: English