Innovative Therapies for Hemoglobin Disorders

by Karine Sii-Felice, Olivier Negre, Christian Brendel, Alisa Tubsuwan, Eglantine Morel-à-l’Huissier, Camille Filardo, Emmanuel Payen
Published 2020

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β^a(T87Q)-Globin Gene

by Olivier Negre, Anne Virginie Eggimann, Yves Beuzard, Jean Antoine Ribeil, Philippe Bourget, Suparerk Borwornpinyo, Suradej Hongeng, Salima Hacein-Bey, Marina Cavazzana, Philippe Leboulch, Emmanuel Payen
Published 2018

Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient

by Alisa Tubsuwan, Soumeya Abed, Annette Deichmann, Melanie D. Kardel, Cynthia Bartholomä, Alice Cheung, Olivier Negre, Zahra Kadri, Suthat Fucharoen, Christof Von Kalle, Emmanuel Payen, Stany Chrétien, Manfred Schmidt, Connie J. Eaves, Philippe Leboulch, Leïla Maouche-Chrétien
Published 2018

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

by Kanit Bhukhai, Edouard de Dreuzy, Marie Giorgi, Charlotte Colomb, Olivier Negre, Maria Denaro, Béatrix Gillet-Legrand, Joëlle Cheuzeville, Anaïs Paulard, Hélène Trebeden-Negre, Suparerk Borwornpinyo, Karine Sii-Felice, Leila Maouche, Julian D. Down, Phillippe Leboulch, Emmanuel Payen
Published 2019