Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice

© 2018 ISEH – Society for Hematology and Stem Cells The β-hemoglobinopathies, transfusion-dependent β-thalassemia and sickle cell disease, are the most prevalent inherited disorders worldwide and affect millions of people. Many of these patients have a shortened life expectancy and suffer from seve...

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Bibliographic Details
Main Authors: Karine Sii-Felice, Marie Giorgi, Philippe Leboulch, Emmanuel Payen
Other Authors: Brigham and Women's Hospital
Format: Article
Published: 2019
Subjects:
Online Access:https://repository.li.mahidol.ac.th/handle/123456789/45101
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Institution: Mahidol University