Therapeutics in paediatric genetic diseases: current and future landscape
There are more than 7,000 paediatric genetic diseases (PGDs) but less than 5% have treatment options. Treatment strategies targeting different levels of the biological process of the disease have led to optimal health outcomes in a subset of patients with PGDs, where treatment is available. In the p...
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Main Authors: | Koh, Ai Ling, Jamuar, Saumya Shekhar |
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Other Authors: | Lee Kong Chian School of Medicine (LKCMedicine) |
Format: | Article |
Language: | English |
Published: |
2023
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Subjects: | |
Online Access: | https://hdl.handle.net/10356/169411 |
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Institution: | Nanyang Technological University |
Language: | English |
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